Medium-Chain Acyl-CoA Dehydrogenase (MCAD) Deficiency (MCADD) Medication

Updated: Mar 31, 2021
  • Author: Karl S Roth, MD; Chief Editor: Luis O Rohena, MD, PhD, FAAP, FACMG  more...
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Medication

Medication Summary

The only appropriate medication is carnitine, although this remains controversial among specialists of inherited biochemical diseases.