Metachromatic Leukodystrophy Medication

Updated: Dec 10, 2019
  • Author: Theodore Moore, MD, MS; Chief Editor: Luis O Rohena, MD, MS, FAAP, FACMG  more...
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Medication Summary

Drug therapy is currently not a component of the standard of care for this disease. Provide supportive care for complications. Recombinant human arylsulfatase A (rhARSA) enzyme is available in Europe and has been designated orphan status in the United States.